A baby's life was saved thanks to a custom gene-editing treatment that was made just for him and designed to fix his precise mutation. This is an incredible achievement!
The therapy was built on decades of federally funded research, and could one day treat millions. But advances like this are at risk due to science funding cuts.
https://apnews.com/article/crispr-gene-editing-rare-disease-mutation-chop-penn-4ab95afadde97164ae6c2450d79acbf8